NewslettersCell Therapy News An Innovative Hematopoietic Stem Cell Gene Therapy Approach Benefits CLN1 Disease in the Mouse Model By Jamie Kang - March 13, 2023 0 Scientists provided evidence of the efficacy and feasibility of a novel approach to treat CLN1 disease and possibly other neurodegenerative conditions, paving the way for its future clinical application. [EMBO Molecular Medicine] Full ArticleGraphical Abstract