Investigators demonstrated that gene therapy reverts the transcriptional signature of Fanconi anemia hematopoietic stem and progenitor cells (HSPCs), which then resembles the transcriptional program of healthy donor HSPCs.
[Haematologica]
Home Newsletters Cell Therapy News Gene Therapy Restores the Transcriptional Program of Hematopoietic Stem Cells in Fanconi...
