NewslettersHematopoiesis News Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia By Noshin Noorjahan - April 26, 2024 0 The authors conducted an open-label, single-group, Phase III study of exa-cel in patients 12 to 35 years of age with transfusion-dependent β-thalassemia and a β0/β0, β0/β0-like, or non–β0/β0-like genotype. [New England Journal Of Medicine] Abstract