NewslettersCell Therapy NewsHematopoiesis NewsAn Empowered, Clinically-Viable Hematopoietic Stem Cell Gene Therapy Approach for the Treatment of Multisystemic Mucopolysaccharidosis Type IIBy Laurisa Dohm - February 6, 2024072Scientists developed up to clinical readiness a new Hematopoietic Stem Cell (HSC) gene therapy approach for Mucopolysaccharidosis type II that benefitted from a novel highly effective transduction protocol.[Molecular Therapy]AbstractGraphical Abstract