Efficacy and Safety of Azacitidine in Pediatric Patients with Newly Diagnosed Advanced Myelodysplastic Syndromes Before Hematopoietic Stem Cell Transplantation in the AZA-JMML-001 Trial

Scientists reported efficacy, pharmacokinetics, and safety data obtained in treatment-naive, pediatric patients with newly diagnosed advanced myelodysplastic syndromes receiving azacitidine in the AZA-JMML-001 study.