Researchers performed a cord blood hematopoietic cell transplantation with a reduced intensity conditioning on a nine-year-boy with adrenoleukodystrophy.
[Molecular Genetics and Metabolism Reports]
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Yada, Y., Torio, M., Koga, Y., Yamashita, F., Ichimura, T., Eguchi, K., Ishimura, M., Mushimoto, Y., Hiwatashi, A., Sasazuki, M., Kira, R., Sakai, Y., & Ohga, S. (2021). Brain-sparing cord blood transplantation for the borderline stage of adrenoleukodystrophy. Molecular Genetics and Metabolism Reports, 28, 100778. https://doi.org/10.1016/j.ymgmr.2021.100778 Cite
