spinal muscular atrophy

[Cure SMA (Globe Newswire, Inc.)] Cure SMA and Cytokinetics announced the renewal of their partnership to increase education, awareness, public policy and fundraising for spinal muscular atrophy (SMA).

[Scholar Rock, Inc.] Scholar Rock, Inc. announced that the FDA has granted Rare Pediatric Disease designation for SRK-015 for the treatment of Spinal Muscular Atrophy, a progressive, rare genetic disease that leads to motor function impairments.