NewslettersMuscle Cell NewsAro Biotherapeutics Receives FDA Orphan Drug Designation for ABX1100 for the Treatment of Pompe DiseaseBy lbeveridge - August 14, 2022046Aro Biotherapeutics announced that the FDA granted Orphan Drug Designation for ABX1100, an investigational Centyrin-siRNA conjugate that targets the Gys1 gene in the muscle, for the treatment of Pompe disease.[Aro Biotherapeutics]Press Release