Continued Improvements in Motor Milestones in Infants with Type I Spinal Muscular Atrophy After Two Years of Treatment with Evrysdi

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PTC Therapeutics, Inc. announced that results from Part II of the pivotal FIREFISH trial demonstrated that infants with type 1 spinal muscular atrophy treated with Evrysdi obtained increases in survival and sustained improvements in achieving key motor milestones, including head control, sitting, rolling over, and further developing towards acquiring the ability to stand, and walk.
[PTC THerapeutics, Inc.]
Press Release